- Gene therapy for cystic fibrosis promising for some patients Updated: Jul-02-15 6:55 pm
LONDON - Doctors who gave children with cystic fibrosis a replacement copy of a defective gene say it appeared to slow the expected decline of some patients' lungs, but called the results "modest" and say there must be major improvements before offering the treatment more widely.
- FDA clears drug for leading form of cystic fibrosis Updated: Jul-02-15 4:54 pm
WASHINGTON - Federal health officials have approved a new combination drug for the most common form of cystic fibrosis, the debilitating inherited disease that causes internal mucus buildup, lung infections and early death. But it will come at a steep price - more than $250,000 for a year's treatment.